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P13271
PAAV2/8
Molecular therapy : the journal of the American Society of Gene Therapy
12.1
2021-05-09

文献信息汇总

Jinkun Wen; Tianqi Cao; Jinni Wu; Yuxi Chen; Shengyao Zhi; Yanming Huang; Peilin Zhen; Guanglan Wu; Lars Aagaard; Jianxin Zhong; Puping Liang; Junjiu Huang,Single AAV-mediated CRISPR-Nme2Cas9 efficiently reduces mutant hTTR expression in a transgenic mouse model of transthyretin amyloidosis,2021-5-9,DOI:10.1016/j.ymthe.2021.05.010,(IF:12.1)
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