文献信息汇总
Jinkun Wen; Tianqi Cao; Jinni Wu; Yuxi Chen; Shengyao Zhi; Yanming Huang; Peilin Zhen; Guanglan Wu; Lars Aagaard; Jianxin Zhong; Puping Liang; Junjiu Huang,Single AAV-mediated CRISPR-Nme2Cas9 efficiently reduces mutant hTTR expression in a transgenic mouse model of transthyretin amyloidosis,2021-5-9,DOI:10.1016/j.ymthe.2021.05.010,(IF:12.1)